Spinal muscular atrophy (SMA) – Market outlook, Epidemiology, Competitive Landscape and Market Forecast Report – 2020 To 2030


 Spinal muscular atrophy (SMA) is a group of inherited disorders characterized by a loss of certain nerve cells in the spinal cord called motor neurons or anterior horn cells.

Etiology-

SMA types 0, 1, 2, 3, and 4 are inherited as autosomal recessive genetic disorders and are associated with abnormalities (mutations) in the SMN1 and SMA2 genes on chromosome 5 at chromosomal locus 5q11-q13. SMA1 is thought to be the primary disease-causing gene.

Epidemiology-

Spinal muscular atrophy affects 1 per 8,000 to 10,000 people worldwide.

The competitive landscape of Spinal muscular atrophy (SMA) includes country-specific approved as well as pipeline therapies. Any asset/product-specific designation or review and Accelerated Approval are being tracked and supplemented with analyst commentary.

KOLs insights of Spinal muscular atrophy (SMA) across 8 MM market from the centre of Excellence/ Public/ Private hospitals participated in the study. Insights around current treatment landscape, epidemiology, clinical characteristics, future treatment paradigm, and Unmet needs.

Spinal muscular atrophy (SMA) Market Forecast: Patient Based Forecast Model (MS. Excel Based Automated Dashboard) which Data Inputs with sourcing, Market Event, and Product Event, Country specific Forecast Model, Market uptake and patient share uptake, Attribute Analysis, Analog Analysis, Disease burden, and pricing scenario, Summary, and Insights.

Read more: Spinal muscular atrophy (SMA) – Market outlook, Epidemiology, Market Forecast and Competitive Landscape Report – 2020 To 2030

S. No    Asset               Company                                 Stage

1          Onasemnogene Abeparvovec-xioi          Novartis Gene Therapies            Phase 3

2          Reldesemtiv      Cytokinetics      Phase 2

3          Nusinersen       Biogen  Phase 3

4          Risdiplam          Hoffmann-La Roche      Phase 2

5          SRK-015           Scholar Rock, Inc.         Phase 2

6          Valproic Acid (VPA)       Abbott  Phase 2

7          Amifampridine Phosphate          Catalyst Pharmaceuticals, Inc.            Phase 2

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