Pseudoxanthoma elasticum (PXE) – Market outlook, Epidemiology, Competitive Landscape, and Market Forecast Report – 2020 To 2030


 Pseudoxanthoma elasticum (PXE) is an inherited metabolic disorder due to ABCC6 gene mutations. It is characterized by progressive calcification and fragmentation of elastic fibers in the skin, retina, and arterial wall. Despite calcium accumulation in the arteries of PXE patients, functional consequences remain unknown.

 

Epidemiology-

According to the literature review conducted by Thelansis, the prevalence of PXE estimated to be 1 in 50,000 would imply that there are ~8,000–10,000 PXE patients in the United States. With the same global prevalence, there could be as many as 160,000 to 200,000 patients affected with PXE worldwide.

 

The competitive landscape of Pseudoxanthoma elasticum (PXE) includes country-specific approved as well as pipeline therapies. Any asset/product-specific designation or review and Accelerated Approval are being tracked and supplemented with analyst commentary.

KOLs insights of Pseudoxanthoma elasticum (PXE) across 8 MM market from the center of Excellence/ Public/ Private hospitals participated in the study. Insights around current treatment landscape, epidemiology, clinical characteristics, future treatment paradigm, and Unmet needs.

Pseudoxanthoma elasticum (PXE) Market Forecast: Patient Based Forecast Model (MS. Excel Based Automated Dashboard) which Data Inputs with sourcing, Market Event, and Product Event, Country specific Forecast Model, Market uptake and patient share uptake, Attribute Analysis, Analog Analysis, Disease burden, and pricing scenario, Summary, and Insights.

Read more: Pseudoxanthoma elasticum (PXE) – Market outlook, Epidemiology, Market Forecast, and Competitive Landscape Report – 2020 To 2030

S. No    Asset               Company                                 Stage

1          INZ-701            Inozyme Pharma, Inc.    Phase 2

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