Pediatric Congenital Athymia – Market outlook, Epidemiology, Competitive Landscape and Market Forecast Report – 2020 To 2030

Pediatric congenital athymia is an ultra-rare immune disorder in which a child is born without a thymus—an organ that plays a critical role in helping the body learn to fight off infections. Multiple genetic abnormalities, congenital syndromes, and environmental factors are being associated, and the care of these infants is complex. While 22q11.2 deletion-associated with DiGeorge Syndrome (DGS) is the most common genetic defect associated with congenital athymia. FOXN1, PAX1, and others have also been identified as potentially causative. Children with congenital athymia may have repeated, often life-threatening infections because they don’t have enough working T cells (infection-fighting white blood cells) to fight them off. It’s important to know that these infections can be fatal.

 

The competitive landscape of Pediatric Congenital Athymia includes country-specific approved and pipeline therapies. Any asset/product-specific designation or review and Accelerated Approval are tracked and supplemented with analyst commentary.

KOLs insights of Pediatric Congenital Athymia across 8 MM market from the centre of Excellence/ Public/ Private hospitals participated in the study. Insights around current treatment landscape, epidemiology, clinical characteristics, future treatment paradigm, and Unmet needs.

Pediatric Congenital Athymia Market Forecast: Patient Based Forecast Model (MS. Excel Based Automated Dashboard) which Data Inputs with sourcing, Market Event, and Product Event, Country specific Forecast Model, Market uptake and patient share uptake, Attribute Analysis, Analog Analysis, Disease burden, and pricing scenario, Summary, and Insights.

Read more: Pediatric Congenital Athymia – Market outlook, Epidemiology, Market Forecast and Competitive Landscape Report – 2020 To 2030

S. No    Asset               Company                                 Stage

1          RETHYMIC®    Enzyvant          Phase 2/3

 

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