Limb-girdle Muscular Dystrophy Type 2i (LGMD2i) – Market outlook, Epidemiology, Competitive Landscape and Market Forecast Report – 2020 To 2030


 Limb-girdle muscular dystrophies (LGMDs) are a group of muscle diseases whose mode of inheritance may be either autosomal dominant (LGMD type 1) or autosomal recessive (LGMD type 2). The fukutin-related protein gene (FKRP; OMIM 606596) is implicated in causing both LGMD2I and congenital muscular dystrophy 1C. The FKRP transcript is expressed predominantly in the skeletal muscle, placenta, and heart. Abnormalities in the expression pattern of the α-dystroglycan protein have been demonstrated in muscle biopsies of LGMD2I patients, indirectly suggesting that FKRP, a putative glycosyltransferase, is required for the post-translational modification of dystroglycan.

The competitive landscape of Limb-girdle Muscular Dystrophy Type 2i (LGMD2i) includes country-specific approved and pipeline therapies. Any asset/product-specific designation or review and Accelerated Approval are tracked and supplemented with analyst commentary.

KOLs insights of Limb-girdle Muscular Dystrophy Type 2i (LGMD2i) across 8 MM market from the centre of Excellence/ Public/ Private hospitals participated in the study. Insights around current treatment landscape, epidemiology, clinical characteristics, future treatment paradigm, and Unmet needs.

Limb-girdle Muscular Dystrophy Type 2i (LGMD2i) Market Forecast: Patient Based Forecast Model (MS. Excel Based Automated Dashboard) which Data Inputs with sourcing, Market Event, and Product Event, Country specific Forecast Model, Market uptake and patient share uptake, Attribute Analysis, Analog Analysis, Disease burden, and pricing scenario, Summary, and Insights.

Read more: Limb-girdle Muscular Dystrophy Type 2i (LGMD2i) – Market outlook, Epidemiology, Market Forecast and Competitive Landscape Report – 2020 To 2030

S. No    Asset               Company                                 Stage

1          BBP-418           ML Bio Solutions, Inc.    Phase 2

2          PF 06252616    Pfizer    Phase 2

3          Deflazacort       PTC Therapeutics         Phase 3

4          BBP-418           BridgeBio Pharma, Inc.  Phase 2

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