Duchenne muscular dystrophy (DMD)– Market outlook, Epidemiology, Competitive Landscape and Market Forecast Report – 2020 To 2030

Duchenne muscular dystrophy (DMD) are a group of genetic conditions characterized by progressive muscle weakness and wasting (atrophy).

Etiology-

DMD is caused by mutations of the DMD gene located on the short arm (p) of the X chromosome (Xp21.2). The DMD gene regulates (encodes for) the production of dystrophin, a protein that appears to play an essential role in maintaining the integrity of cell membrane in skeletal (voluntary) and cardiac muscle cells

Epidemiology-

Affecting approximately 1 in 3,500 male births worldwide and estimated to affect 250,000 individuals in the United States.

 

The competitive landscape of Duchenne muscular dystrophy (DMD) includes country-specific approved as well as pipeline therapies. Any asset/product-specific designation or review and Accelerated Approval are being tracked and supplemented with analyst commentary.

KOLs insights of Duchenne muscular dystrophy (DMD) across 8 MM market from the center of Excellence/ Public/ Private hospitals participated in the study. Insights around current treatment landscape, epidemiology, clinical characteristics, future treatment paradigm, and Unmet needs.

Duchenne muscular dystrophy (DMD) Market Forecast: Patient Based Forecast Model (MS. Excel Based Automated Dashboard) which Data Inputs with sourcing, Market Event, and Product Event, Country specific Forecast Model, Market uptake and patient share uptake, Attribute Analysis, Analog Analysis, Disease burden, and pricing scenario, Summary, and Insights.

Read more: Duchenne muscular dystrophy (DMD)– Market outlook, Epidemiology, Market Forecast and Competitive Landscape Report – 2020 To 2030

S. No    Asset               Company                                 Stage

1          SRP-9001         Sarepta Therapeutics, Inc.         Phase 3

2          ITF2357            Italfarmaco       Phase 1

3          Viltolarsen         NS Pharma, Inc.            Phase 3

4          Pamrevlumab    FibroGen          Phase 3

5          Bocidelpar         Astellas Pharma Inc      Phase 1

6          Vamorolone      ReveraGen BioPharma, Inc.      Phase 2

7          DS-5141b         Daiichi Sankyo Co., Ltd. Phase 2

8          WVE-N531        Wave Life Sciences Ltd. Phase 1/2

9          TAS-205           Taiho Pharmaceutical Co., Ltd.  Phase 3

10        SGT-001           Solid Biosciences, LLC  Phase 1/2

Continued...

 

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