Batten disease – Market outlook, Epidemiology, Competitive Landscape and Market Forecast Report – 2020 To 2030


 Batten disease – Market outlook, Epidemiology, Market Forecast and Competitive Landscape Report – 2020 To 2030 (Markets covered: US, Germany, France, Spain, United Kingdom, Italy, Japan & China).

Batten disease is the common name for a broad class of rare, fatal, inherited disorders of the nervous system also known as neuronal ceroid lipofuscinoses, or NCLs.

Etiology-

Batten disease is an inherited genetic disorder that appears to affect the function of tiny bodies within cells called lysosomes. In Batten disease/NCLs, the mutated genes do not produce the proper amounts of proteins important for lysosomal function.

Epidemiology-

Batten Disease and other forms of NCL are relatively rare, occurring in an estimated 2 to 4 of every 100,000 births in the United States.

The competitive landscape of Batten disease includes country-specific approved as well as pipeline therapies. Any asset/product-specific designation or review and Accelerated Approval are being tracked and supplemented with analyst commentary.

KOLs insights of Batten disease across 8 MM market from the center of Excellence/ Public/ Private hospitals participated in the study. Insights around current treatment landscape, epidemiology, clinical characteristics, future treatment paradigm, and Unmet needs.

Batten disease Market Forecast: Patient Based Forecast Model (MS. Excel Based Automated Dashboard) which Data Inputs with sourcing, Market Event, and Product Event, Country specific Forecast Model, Market uptake and patient share uptake, Attribute Analysis, Analog Analysis, Disease burden, and pricing scenario, Summary, and Insights.

Read more: Batten disease – Market outlook, Epidemiology, Market Forecast and Competitive Landscape Report – 2020 To 2030

S. No    Asset               Company                                 Stage

1          AT-GTX-502     Amicus Therapeutics     Phase 2

2          PLX-200           Polaryx Therapeutics, Inc.         Phase 3

3          BMN 190          BioMarin Pharmaceutical           Phase 2

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