Limb-Girdle Muscular Dystrophy Type 2 – Market outlook, Epidemiology, Competitive Landscape, and Market Forecast Report – 2020 To 2030


 Limb-Girdle Muscular Dystrophy Type 2 (LGMD2A, LGMD2B, LGMD2C, LGMD2D, LGMD2E, LGMD2F, LGMD2G, LGMD2I, LGMD2J, LGMD2L, Others (LGMD2H, LGMD2K, LGMD2M-Z)) includes forms of autosomal recessive characterized by progressive weakness of the muscles of the pelvic girdle, legs, arms, and shoulders. Progression of muscle weakness may be slow or rapid and may vary even among individuals in the same family. Intelligence is normal. The age of onset ranges from subgroup to subgroup. Overall, the beginning is more common in childhood, but it may occur in adulthood. Diagnosis of LGMD2A is complicated by phenotypic variability, lack of precise protein analysis, and absence of mutational hot spots in the CAPN3 gene. Children between the ages of 8-and 15 may range from 2-to 40 years of age. Most cases are characterized by muscle .weakness affecting the hip-girdle area, although the hip adductor muscles may be spared.

The prevalence of Limb-girdle muscular dystrophy type 2 varies from 47 to 53 cases per million in the USA.

 

The competitive landscape of Limb-Girdle Muscular Dystrophy Type 2 includes country-specific approved and pipeline therapies. Any asset/product-specific designation or review and Accelerated Approval are tracked and supplemented with analyst commentary.

KOLs insights of Limb-Girdle Muscular Dystrophy Type 2 across 8 MM market from the center of Excellence/ Public/ Private hospitals participated in the study. Insights around current treatment landscape, epidemiology, clinical characteristics, future treatment paradigm, and Unmet needs.

Limb-Girdle Muscular Dystrophy Type 2 Market Forecast: Patient Based Forecast Model (MS. Excel Based Automated Dashboard), which Data Inputs with sourcing, Market Event, and Product Event, Country specific Forecast Model, Market uptake and patient share uptake, Attribute Analysis, Analog Analysis, Disease burden, and pricing scenario, Summary, and Insights.

Read more: Limb-Girdle Muscular Dystrophy Type 2 – Market outlook, Epidemiology, Market Forecast, and Competitive Landscape Report – 2020 To 2030

S. No    Asset               Company                                 Stage

1          ATA-100           Atamyo Therapeutics     Phase 1

2          Deflazacort       PTC Therapeutics         Phase 3

3          LION-101          Asklepios Biopharmaceutical, Inc.          Phase 2

4          SRP-9003         Sarepta Therapeutics, Inc.         Phase 1

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