Prader-Willi syndrome – Market outlook, Epidemiology, Competitive Landscape, and Market Forecast Report – 2020 To 2030
Prader–Willi syndrome is a genetic disorder due to the loss of function of specific genes. In newborns, symptoms include weak muscles, poor feeding, and slow development. Beginning in childhood, the person becomes constantly hungry, which often leads to obesity and T2D.
·
Patients with Prader-Willi
syndrome frequently reach adulthood and are able to function in a group home
setting, performing vocational work, or attending community college classes.
Diminished sensitivity to pain and diminished capacity to vomit may delay the
diagnosis of underlying disease
·
According to Thelansis’s
research prevalence at birth is estimated at 1/15,000-30,000 worldwide. Most
estimates place the incidence between 1 in 10,000-30,000 individuals in the
general population and about 350,000-400,000 individuals worldwide. PWS affects
males and females in equal numbers and occurs in all ethnic groups and
geographic regions in the world
· Although specific treatments vary depending on
symptoms, most children with PWS will need the following: good nutrition for
infants, Human growth hormone (HGH) treatment, sex hormone treatment, weight
management, treatment of sleep disturbances, etc.
The competitive
landscape of Prader-Willi syndrome includes country-specific approved and
pipeline therapies. Any asset/product-specific designation or review and
Accelerated Approval are tracked and supplemented with analyst commentary.
KOLs insights of Prader-Willi
syndrome across 8 MM market from the center of Excellence/ Public/ Private
hospitals participated in the study. Insights around current treatment
landscape, epidemiology, clinical characteristics, future treatment paradigm,
and Unmet needs.
Prader-Willi
syndrome Market
Forecast: Patient Based Forecast Model (MS. Excel Based Automated
Dashboard) which Data Inputs with sourcing, Market Event, and Product Event,
Country specific Forecast Model, Market uptake and patient share uptake,
Attribute Analysis, Analog Analysis, Disease burden, and pricing scenario,
Summary, and Insights.
S. No Asset Company Stage
1 NNZ-2591 Neuren
Pharmaceuticals Phase 1
2 intranasal carbetocin Dose 1 Levo Therapeutics, Inc. Phase
3
3 RM-493 Rhythm Pharmaceuticals,
Inc. Phase 2
4 Pitolisant oral tablets Harmony
Biosciences, LLC Phase 2
5 rhGH GeneScience
Pharmaceuticals Co., Ltd. Phase 3
6 Eutropin LG
Life Sciences Phase 3
7 Tesofensine/Metoprolol Saniona Phase 2
8 somatropin - GH naïve pediatric cohort Pfizer Phase
3
9 FE 992097 Ferring
Pharmaceuticals Phase 2
10 ZGN-440 Zafgen,
Inc. Phase 2
Continued..
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